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High-throughput transcriptome analyses from ASPIRO, a phase 1/2/3 study of gene replacement therapy for X-linked myotubular myopathy |
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Titel: |
High-throughput transcriptome analyses from ASPIRO, a phase 1/2/3 study of gene replacement therapy for X-linked myotubular myopathy |
Auteur: |
Andreoletti, Gaia Romano, Oriana Chou, Hsin-Jung Sefid-Dashti, Mahjoubeh J. Grilli, Andrea Chen, Clarice Lakshman, Neema Purushothaman, Pravin Varfaj, Fatbardha Mavilio, Fulvio Bicciato, Silvio Urbinati, Fabrizia |
Verschenen in: |
The American journal of human genetics |
Paginering: |
Jaargang 110 () nr. 10 pagina's 1648-1660 |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
American Society of Human Genetics |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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