Gene Augmentation and Readthrough Rescue Channelopathy in an iPSC-RPE Model of Congenital Blindness
Titel:
Gene Augmentation and Readthrough Rescue Channelopathy in an iPSC-RPE Model of Congenital Blindness
Auteur:
Shahi, Pawan K. Hermans, Dalton Sinha, Divya Brar, Simran Moulton, Hannah Stulo, Sabrina Borys, Katarzyna D. Capowski, Elizabeth Pillers, De-Ann M. Gamm, David M. Pattnaik, Bikash R.