GLA-modified RNA treatment lowers GB3 levels in iPSC-derived cardiomyocytes from Fabry-affected individuals
Titel:
GLA-modified RNA treatment lowers GB3 levels in iPSC-derived cardiomyocytes from Fabry-affected individuals
Auteur:
ter Huurne, Menno Parker, Benjamin L. Liu, Ning Qing Qian, Elizabeth Ling Vivien, Celine Karavendzas, Kathy Mills, Richard J. Saville, Jennifer T. Abu-Bonsrah, Dad Wise, Andrea F. Hudson, James E. Talbot, Andrew S. Finn, Patrick F. Martini, Paolo G.V. Fuller, Maria Ricardo, Sharon D. Watt, Kevin I. Nicholls, Kathy M. Porrello, Enzo R. Elliott, David A.