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Modified lentiviral globin gene therapy for pediatric β0/β0 transfusion-dependent β-thalassemia: A single-center, single-arm pilot trial |
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Titel: |
Modified lentiviral globin gene therapy for pediatric β0/β0 transfusion-dependent β-thalassemia: A single-center, single-arm pilot trial |
Auteur: |
Li, Shiqi Ling, Sikai Wang, Dawei Wang, Xiaoyuan Hao, Fangyuan Yin, Liufan Yuan, Zhongtao Liu, Lin Zhang, Lin Li, Yu Chen, Yingnian Luo, Le Dai, Ying Zhang, Lihua Chen, Lvzhe Deng, Dongjie Tang, Wei Zhang, Sujiang Wang, Sanbin Cai, Yujia |
Verschenen in: |
Cell stem cell |
Paginering: |
Jaargang 31 () nr. 7 pagina's 961-973.e8 |
Jaar: |
2024 |
Inhoud: |
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Uitgever: |
The Authors |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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