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Base editing of the HBG promoter induces potent fetal hemoglobin expression with no detectable off-target mutations in human HSCs |
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Titel: |
Base editing of the HBG promoter induces potent fetal hemoglobin expression with no detectable off-target mutations in human HSCs |
Auteur: |
Han, Wenyan Qiu, Hou-Yuan Sun, Shangwu Fu, Zhi-Can Wang, Guo-Quan Qian, Xiaowen Wang, Lijie Zhai, Xiaowen Wei, Jia Wang, Yichuan Guo, Yi-Lin Cao, Guo-Hua Ji, Rui-Jin Zhang, Yi-Zhou Ma, Hongxia Wang, Hongsheng Zhao, Mingli Wu, Jing Bi, Lili Chen, Qiu-Bing Li, Zifeng Yu, Ling Mou, Xiaodun Yin, Hao Yang, Li Chen, Jia Yang, Bei Zhang, Ying |
Verschenen in: |
Cell stem cell |
Paginering: |
Jaargang 30 () nr. 12 pagina's 1624-1639.e8 |
Jaar: |
2023 |
Inhoud: |
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Uitgever: |
Elsevier Inc. |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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