High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia
Titel:
High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia
Auteur:
Vaidyanathan, Sriram Salahudeen, Ameen A. Sellers, Zachary M. Bravo, Dawn T. Choi, Shannon S. Batish, Arpit Le, Wei Baik, Ron de la O, Sean Kaushik, Milan P. Galper, Noah Lee, Ciaran M. Teran, Christopher A. Yoo, Jessica H. Bao, Gang Chang, Eugene H. Patel, Zara M. Hwang, Peter H. Wine, Jeffrey J. Milla, Carlos E. Desai, Tushar J. Nayak, Jayakar V. Kuo, Calvin J. Porteus, Matthew H.