A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
Titel:
A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells
Auteur:
Young, Courtney S. Hicks, Michael R. Ermolova, Natalia V. Nakano, Haruko Jan, Majib Younesi, Shahab Karumbayaram, Saravanan Kumagai-Cresse, Chino Wang, Derek Zack, Jerome A. Kohn, Donald B. Nakano, Atsushi Nelson, Stanley F. Miceli, M. Carrie Spencer, Melissa J. Pyle, April D.