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Expression of a Secretable, Cell-Penetrating CDKL5 Protein Enhances the Efficacy of Gene Therapy for CDKL5 Deficiency Disorder |
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Titel: |
Expression of a Secretable, Cell-Penetrating CDKL5 Protein Enhances the Efficacy of Gene Therapy for CDKL5 Deficiency Disorder |
Auteur: |
Medici, Giorgio Tassinari, Marianna Galvani, Giuseppe Bastianini, Stefano Gennaccaro, Laura Loi, Manuela Mottolese, Nicola Alvente, Sara Berteotti, Chiara Sagona, Giulia Lupori, Leonardo Candini, Giulia Baggett, Helen Rappe Zoccoli, Giovanna Giustetto, Maurizio Muotri, Alysson Pizzorusso, Tommaso Nakai, Hiroyuki Trazzi, Stefania Ciani, Elisabetta |
Verschenen in: |
Neurotherapeutics |
Paginering: |
Jaargang 19 () nr. 6 pagina's 1886-1904 |
Jaar: |
2022-09-15 |
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Uitgever: |
Springer International Publishing, Cham |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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