CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease phenotypes in a kidney organoid model
Titel:
CRISPR/Cas9-mediated A4GALT suppression rescues Fabry disease phenotypes in a kidney organoid model
Auteur:
Cui, Sheng Shin, Yoo Jin Fang, Xianying Lee, Hanbi Eum, Sang Hun Ko, Eun Jeong Lim, Sun Woo Shin, Eunji Lee, Kang In Lee, Jae Young Lee, Chae Bin Bae, Soo Kyung Yang, Chul Woo Chung, Byung Ha