Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice
Titel:
Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice
Auteur:
Benhamida, Sonia Pflumio, Françoise Dubart-Kupperschmitt, Anne Zhao-Emonet, Jing-Chao Cavazzana-Calvo, Marina Rocchiccioli, Francis Fichelson, Serge Aubourg, Patrick Charneau, Pierre Cartier, Nathalie