Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy
Titel:
Combination HSCT and intravenous AAV-mediated gene therapy in a canine model proves pivotal for translation of Krabbe disease therapy
Auteur:
Bradbury, Allison M. Bagel, Jessica Swain, Gary Miyadera, Keiko Pesayco, Jill P. Assenmacher, Charles-Antoine Brisson, Becky Hendricks, Ian Wang, Xiao H. Herbst, Zachary Pyne, Nettie Odonnell, Patricia Shelton, G. Diane Gelb, Michael Hackett, Neil Szabolcs, Paul Vite, Charles H. Escolar, Maria