Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates
Title:
Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates
Author:
Powers, Samantha Likhite, Shibi Gadalla, Kamal K. Miranda, Carlos J. Huffenberger, Amy J. Dennys, Cassandra Foust, Kevin D. Morales, Pablo Pierson, Christopher R. Rinaldi, Federica Perry, Stephanie Bolon, Brad Wein, Nicolas Cobb, Stuart Kaspar, Brian K. Meyer, Kathrin C.