Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor
Titel:
Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor
Auteur:
Amistadi, Simone Maule, Giulia Ciciani, Matteo Ensinck, Marjolein M. De Keersmaecker, Liesbeth Ramalho, Anabela S. Guidone, Daniela Buccirossi, Martina Galietta, Luis J.V. Carlon, Marianne S. Cereseto, Anna