Extracellular vesicle-based delivery of silencing sequences for the treatment of Machado-Joseph disease/spinocerebellar ataxia type 3
Titel:
Extracellular vesicle-based delivery of silencing sequences for the treatment of Machado-Joseph disease/spinocerebellar ataxia type 3
Auteur:
Rufino-Ramos, David Albuquerque, Patrícia R. Leandro, Kevin Carmona, Vitor Martins, Inês M. Fernandes, Rita Henriques, Carina Lobo, Diana Faro, Rosário Perfeito, Rita Mendonça, Liliana S. Pereira, Dina Gomes, Célia M. Nobre, Rui Jorge Pereira de Almeida, Luís