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Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model |
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Title: |
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model |
Author: |
Bersani, Margherita Rizzuti, Mafalda Pagliari, Elisa Garbellini, Manuela Saccomanno, Domenica Moulton, Hong M. Bresolin, Nereo Comi, Giacomo P. Corti, Stefania Nizzardo, Monica |
Appeared in: |
Molecular therapy |
Paging: |
Volume 30 () nr. 3 pages 1288-1299 |
Year: |
2022 |
Contents: |
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Publisher: |
The Authors |
Source file: |
Elektronische Wetenschappelijke Tijdschriften |
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