Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease
Titel:
Combination of lentiviral and genome editing technologies for the treatment of sickle cell disease
Auteur:
Ramadier, Sophie Chalumeau, Anne Felix, Tristan Othman, Nadia Aknoun, Sherazade Casini, Antonio Maule, Giulia Masson, Cecile De Cian, Anne Frati, Giacomo Brusson, Megane Concordet, Jean-Paul Cavazzana, Marina Cereseto, Anna El Nemer, Wassim Amendola, Mario Wattellier, Benoit Meneghini, Vasco Miccio, Annarita