In Vivo Treatment of Hemophilia A and Mucopolysaccharidosis Type VII Using Nonprimate Lentiviral Vectors
Title:
In Vivo Treatment of Hemophilia A and Mucopolysaccharidosis Type VII Using Nonprimate Lentiviral Vectors
Author:
Stein, Colleen S. Kang, Yubin Sauter, Sybille L. Townsend, Kay Staber, Patrick Derksen, Todd A. Martins, InĂªs Qian, Jiahua Davidson, Beverly L. McCray Jr., Paul B.