Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B
Titel:
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B
Auteur:
George, Lindsey A. Ragni, Margaret V. Rasko, John E.J. Raffini, Leslie J. Samelson-Jones, Benjamin J. Ozelo, Margareth Hazbon, Maria Runowski, Alexa R. Wellman, Jennifer A. Wachtel, Katie Chen, Yifeng Anguela, Xavier M. Kuranda, Klaudia Mingozzi, Federico High, Katherine A.