Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice
Titel:
Pronounced Therapeutic Benefit of a Single Bidirectional AAV Vector Administered Systemically in Sandhoff Mice
Auteur:
Lahey, Hannah G. Webber, Chelsea J. Golebiowski, Diane Izzo, Cassandra M. Horn, Erin Taghian, Toloo Rodriguez, Paola Batista, Ana Rita Ellis, Lauren E. Hwang, Misako Martin, Douglas R. Gray-Edwards, Heather Sena-Esteves, Miguel