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dCas9-Based Scn1a Gene Activation Restores Inhibitory Interneuron Excitability and Attenuates Seizures in Dravet Syndrome Mice |
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Titel: |
dCas9-Based Scn1a Gene Activation Restores Inhibitory Interneuron Excitability and Attenuates Seizures in Dravet Syndrome Mice |
Auteur: |
Colasante, Gaia Lignani, Gabriele Brusco, Simone Di Berardino, Claudia Carpenter, Jenna Giannelli, Serena Valassina, Nicholas Bido, Simone Ricci, Raffaele Castoldi, Valerio Marenna, Silvia Church, Timothy Massimino, Luca Morabito, Giuseppe Benfenati, Fabio Schorge, Stephanie Leocani, Letizia Kullmann, Dimitri M. Broccoli, Vania |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 28 () nr. 1 pagina's 235-253 |
Jaar: |
2020 |
Inhoud: |
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Uitgever: |
The American Society of Gene and Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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