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Non-viral Gene Therapy for Stargardt Disease with ECO/pRHO-ABCA4 Self-Assembled Nanoparticles |
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Titel: |
Non-viral Gene Therapy for Stargardt Disease with ECO/pRHO-ABCA4 Self-Assembled Nanoparticles |
Auteur: |
Sun, Da Schur, Rebecca M. Sears, Avery E. Gao, Song-Qi Vaidya, Amita Sun, Wenyu Maeda, Akiko Kern, Timothy Palczewski, Krzysztof Lu, Zheng-Rong |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 28 () nr. 1 pagina's 293-303 |
Jaar: |
2020 |
Inhoud: |
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Uitgever: |
The American Society of Gene and Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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