Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing
Titel:
Clinically Relevant Correction of Recessive Dystrophic Epidermolysis Bullosa by Dual sgRNA CRISPR/Cas9-Mediated Gene Editing
Auteur:
Bonafont, Jose Mencía, Ángeles García, Marta Torres, Raúl Rodríguez, Sandra Carretero, Marta Chacón-Solano, Esteban Modamio-Høybjør, Silvia Marinas, Lucía León, Carlos Escamez, María J. Hausser, Ingrid Del Río, Marcela Murillas, Rodolfo Larcher, Fernando