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Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression |
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Titel: |
Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression |
Auteur: |
Vidal, Patrice Pagliarani, Serena Colella, Pasqualina Costa Verdera, Helena Jauze, Louisa Gjorgjieva, Monika Puzzo, Francesco Marmier, Solenne Collaud, Fanny Simon Sola, Marcelo Charles, Severine Lucchiari, Sabrina van Wittenberghe, Laetitia Vignaud, Alban Gjata, Bernard Richard, Isabelle Laforet, Pascal Malfatti, Edoardo Mithieux, Gilles Rajas, Fabienne Comi, Giacomo Pietro Ronzitti, Giuseppe Mingozzi, Federico |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 26 () nr. 3 pagina's 890-901 |
Jaar: |
2018 |
Inhoud: |
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Uitgever: |
The American Society of Gene and Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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