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Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice |
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Titel: |
Gene Therapy with BMN 270 Results in Therapeutic Levels of FVIII in Mice and Primates and Normalization of Bleeding in Hemophilic Mice |
Auteur: |
Bunting, Stuart Zhang, Lening Xie, Lin Bullens, Sherry Mahimkar, Rajeev Fong, Sylvia Sandza, Krystal Harmon, Danielle Yates, Bridget Handyside, Britta Sihn, Choong-Ryoul Galicia, Nicole Tsuruda, Laurie O’Neill, Charles A. Bagri, Anil Colosi, Peter Long, Shinong Vehar, Gordon Carter, Barrie |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 26 (2018) nr. 2 pagina's 496-509 |
Jaar: |
2018 |
Inhoud: |
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Uitgever: |
BioMarin Pharmaceutical Inc |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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