Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs
Titel:
Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs
Auteur:
Mack, David L. Poulard, Karine Goddard, Melissa A. Latournerie, Virginie Snyder, Jessica M. Grange, Robert W. Elverman, Matthew R. Denard, Jérôme Veron, Philippe Buscara, Laurine Le Bec, Christine Hogrel, Jean-Yves Brezovec, Annie G. Meng, Hui Yang, Lin Liu, Fujun O’Callaghan, Michael Gopal, Nikhil Kelly, Valerie E. Smith, Barbara K. Strande, Jennifer L. Mavilio, Fulvio Beggs, Alan H. Mingozzi, Federico Lawlor, Michael W. Buj-Bello, Ana Childers, Martin K.