Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model
Titel:
Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model
Auteur:
Gray-Edwards, Heather L. Regier, Debra S. Shirley, Jamie L. Randle, Ashley N. Salibi, Nouha Thomas, Sarah E. Latour, Yvonne L. Johnston, Jean Golas, Gretchen Maguire, Annie S. Taylor, Amanda R. Sorjonen, Donald C. McCurdy, Victoria J. Christopherson, Peter W. Bradbury, Allison M. Beyers, Ronald J. Johnson, Aime K. Brunson, Brandon L. Cox, Nancy R. Baker, Henry J. Denney, Thomas S. Sena-Esteves, Miguel Tifft, Cynthia J. Martin, Douglas R.