|
Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy |
|
|
|
Titel: |
Quantitative Antisense Screening and Optimization for Exon 51 Skipping in Duchenne Muscular Dystrophy |
Auteur: |
Echigoya, Yusuke Lim, Kenji Rowel Q. Trieu, Nhu Bao, Bo Miskew Nichols, Bailey Vila, Maria Candida Novak, James S. Hara, Yuko Lee, Joshua Touznik, Aleksander Mamchaoui, Kamel Aoki, Yoshitsugu Takeda, Shin’ichi Nagaraju, Kanneboyina Mouly, Vincent Maruyama, Rika Duddy, William Yokota, Toshifumi |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 25 (2017) nr. 11 pagina's 2561-2572 |
Jaar: |
2017 |
Inhoud: |
|
Uitgever: |
The American Society of Gene and Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
|
|
|
|