CRISPR/Cas9-Induced (CTG⋅CAG)n Repeat Instability in the Myotonic Dystrophy Type 1 Locus: Implications for Therapeutic Genome Editing
Titel:
CRISPR/Cas9-Induced (CTG⋅CAG)n Repeat Instability in the Myotonic Dystrophy Type 1 Locus: Implications for Therapeutic Genome Editing
Auteur:
van Agtmaal, Ellen L. André, Laurène M. Willemse, Marieke Cumming, Sarah A. van Kessel, Ingeborg D.G. van den Broek, Walther J.A.A. Gourdon, Geneviève Furling, Denis Mouly, Vincent Monckton, Darren G. Wansink, Derick G. Wieringa, Bé