Optimization of Morpholino Antisense Oligonucleotides Targeting the Intronic Repressor Element1 in Spinal Muscular Atrophy
Titel:
Optimization of Morpholino Antisense Oligonucleotides Targeting the Intronic Repressor Element1 in Spinal Muscular Atrophy
Auteur:
Osman, Erkan Y Washington III, Charles W Kaifer, Kevin A Mazzasette, Chiara Patitucci, Teresa N Florea, Kyra M Simon, Madeline E Ko, Chien-Ping Ebert, Allison D Lorson, Christian L