Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Titel:
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Auteur:
Garcia-Gomez, Maria Calabria, Andrea Garcia-Bravo, Maria Benedicenti, Fabrizio Kosinski, Penelope López-Manzaneda, Sergio Hill, Collin del Mar Mañu-Pereira, María Martín, Miguel A Orman, Israel Vives-Corrons, Joan-LLuis Kung, Charles Schambach, Axel Jin, Shengfang Bueren, Juan A Montini, Eugenio Navarro, Susana Segovia, Jose C