Rescue of a Mouse Model of Spinal Muscular Atrophy With Respiratory Distress Type 1 by AAV9-IGHMBP2 Is Dose Dependent
Titel:
Rescue of a Mouse Model of Spinal Muscular Atrophy With Respiratory Distress Type 1 by AAV9-IGHMBP2 Is Dose Dependent
Auteur:
Shababi, Monir Feng, Zhihua Villalon, Eric Sibigtroth, Christine M Osman, Erkan Y Miller, Madeline R Williams-Simon, Patricka A Lombardi, Abby Sass, Thalia H Atkinson, Arleigh K Garcia, Michael L Ko, Chien-Ping Lorson, Christian L