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Coformulation of a Novel Human α-Galactosidase A With the Pharmacological Chaperone AT1001 Leads to Improved Substrate Reduction in Fabry Mice |
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Titel: |
Coformulation of a Novel Human α-Galactosidase A With the Pharmacological Chaperone AT1001 Leads to Improved Substrate Reduction in Fabry Mice |
Auteur: |
Xu, Su Lun, Yi Brignol, Nastry Hamler, Rick Schilling, Adriane Frascella, Michelle Sullivan, Sean Boyd, Robert E Chang, Kate Soska, Rebecca Garcia, Anadina Feng, Jessie Yasukawa, Hidehito Shardlow, Carole Churchill, Alison Ketkar, Amol Robertson, Nicola Miyamoto, Masahito Mihara, Kazutoshi Benjamin, Elfrida R Lockhart, David J Hirato, Tohru Fowles, Susie Valenzano, Kenneth J Khanna, Richie |
Verschenen in: |
Molecular therapy |
Paginering: |
Jaargang 23 (2015) nr. 7 pagina's 13 p. |
Jaar: |
2015 |
Inhoud: |
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Uitgever: |
American Society of Gene & Cell Therapy |
Bronbestand: |
Elektronische Wetenschappelijke Tijdschriften |
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