Long-Term Correction of Sandhoff Disease Following Intravenous Delivery of rAAV9 to Mouse Neonates
Titel:
Long-Term Correction of Sandhoff Disease Following Intravenous Delivery of rAAV9 to Mouse Neonates
Auteur:
Walia, Jagdeep S Altaleb, Naderah Bello, Alexander Kruck, Christa LaFave, Matthew C Varshney, Gaurav K Burgess, Shawn M Chowdhury, Biswajit Hurlbut, David Hemming, Richard Kobinger, Gary P Triggs-Raine, Barbara