Huntingtin Haplotypes Provide Prioritized Target Panels for Allele-specific Silencing in Huntington Disease Patients of European Ancestry
Titel:
Huntingtin Haplotypes Provide Prioritized Target Panels for Allele-specific Silencing in Huntington Disease Patients of European Ancestry
Auteur:
Kay, Chris Collins, Jennifer A Skotte, Niels H Southwell, Amber L Warby, Simon C Caron, Nicholas S Doty, Crystal N Nguyen, Betty Griguoli, Annamaria Ross, Colin J Squitieri, Ferdinando Hayden, Michael R