Alpharetroviral Vector-mediated Gene Therapy for X-CGD: Functional Correction and Lack of Aberrant Splicing
Titel:
Alpharetroviral Vector-mediated Gene Therapy for X-CGD: Functional Correction and Lack of Aberrant Splicing
Auteur:
Kaufmann, Kerstin B. Brendel, Christian Suerth, Julia D. Mueller-Kuller, Uta Chen-Wichmann, Linping Schwäble, Joachim Pahujani, Shweta Kunkel, Hana Schambach, Axel Baum, Christopher Grez, Manuel