A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice
Titel:
A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice
Auteur:
Ahmed, Seemin Seher Li, Huapeng Cao, Chunyan Sikoglu, Elif M Denninger, Andrew R Su, Qin Eaton, Samuel Liso Navarro, Ana A Xie, Jun Szucs, Sylvia Zhang, Hongwei Moore, Constance Kirschner, Daniel A Seyfried, Thomas N Flotte, Terence R Matalon, Reuben Gao, Guangping