Preclinical Safety and Efficacy of Human CD34+ Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome
Titel:
Preclinical Safety and Efficacy of Human CD34+ Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome
Auteur:
Scaramuzza, Samantha Biasco, Luca Ripamonti, Anna Castiello, Maria C Loperfido, Mariana Draghici, Elena Hernandez, Raisa J Benedicenti, Fabrizio Radrizzani, Marina Salomoni, Monica Ranzani, Marco Bartholomae, Cynthia C Vicenzi, Elisa Finocchi, Andrea Bredius, Robbert Bosticardo, Marita Schmidt, Manfred von Kalle, Christof Montini, Eugenio Biffi, Alessandra Roncarolo, Maria G Naldini, Luigi Villa, Anna Aiuti, Alessandro