Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector
Titel:
Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector
Auteur:
Bowles, Dawn E McPhee, Scott WJ Li, Chengwen Gray, Steven J Samulski, Jade J Camp, Angelique S Li, Juan Wang, Bing Monahan, Paul E Rabinowitz, Joseph E Grieger, Joshua C Govindasamy, Lakshmanan Agbandje-McKenna, Mavis Xiao, Xiao Samulski, R Jude