Gene Transfer of Low Levels of β-Glucuronidase Corrects Hepatic Lysosomal Storage in a Large Animal Model of Mucopolysaccharidosis VII
Titel:
Gene Transfer of Low Levels of β-Glucuronidase Corrects Hepatic Lysosomal Storage in a Large Animal Model of Mucopolysaccharidosis VII
Auteur:
Wolfe, John H. Sands, Mark S. Harel, Noam Weil, Margaret A. Parente, Micheal K. Polesky, Aracelis C. Reilly, John J. Hasson, Christopher Weimelt, Staci Haskins, Mark E.