Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins
Titel:
Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins
Auteur:
Nathwani, Amit C Rosales, Cecilia McIntosh, Jenny Rastegarlari, Ghasem Nathwani, Devhrut Raj, Deepak Nawathe, Sushmita Waddington, Simon N Bronson, Roderick Jackson, Scott Donahue, Robert E High, Katherine A Mingozzi, Federico Ng, Catherine YC Zhou, Junfang Spence, Yunyu McCarville, M Beth Valentine, Marc Allay, James Coleman, John Sleep, Susan Gray, John T Nienhuis, Arthur W Davidoff, Andrew M