Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors
Titel:
Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors
Auteur:
Sabatino, Denise E Lange, Amy M Altynova, Ekaterina S Sarkar, Rita Zhou, Shangzhen Merricks, Elizabeth P Franck, Helen G Nichols, Timothy C Arruda, Valder R Kazazian Jr, Haig H