Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice
Titel:
Sustained Enzymatic Correction by rAAV-Mediated Liver Gene Therapy Protects Against Induced Motor Neuropathy in Acute Porphyria Mice
Auteur:
Unzu, Carmen Sampedro, Ana Mauleón, Itsaso Alegre, Manuel Beattie, Stuart G de Salamanca, Rafael Enríquez Snapper, Jolanda Twisk, Jaap Petry, Harald González-Aseguinolaza, Gloria Artieda, Julio Rodríguez-Pena, María Sol Prieto, Jesús Fontanellas, Antonio