Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques
Titel:
Stable Human FIX Expression After 0.9G Intrauterine Gene Transfer of Self-complementary Adeno-associated Viral Vector 5 and 8 in Macaques
Auteur:
Mattar, Citra NZ Nathwani, Amit C Waddington, Simon N Dighe, Niraja Kaeppel, Christine Nowrouzi, Ali Mcintosh, Jenny Johana, Nuryanti B Ogden, Bryan Fisk, Nicholas M Davidoff, Andrew M David, Anna Peebles, Donald Valentine, Marcus B Appelt, Jens-Uwe von Kalle, Christof Schmidt, Manfred Biswas, Arijit Choolani, Mahesh Chan, Jerry KY