Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs
Titel:
Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs
Auteur:
Haurigot, Virginia Mingozzi, Federico Buchlis, George Hui, Daniel J Chen, Yifeng Basner-Tschakarjan, Etiena Arruda, Valder R Radu, Antoneta Franck, Helen G Wright, J Fraser Zhou, Shangzhen Stedman, Hansell H Bellinger, Dwight A Nichols, Timothy C High, Katherine A