Preclinical PK and PD Studies on 2′-O-Methyl-phosphorothioate RNA Antisense Oligonucleotides in the mdx Mouse Model
Titel:
Preclinical PK and PD Studies on 2′-O-Methyl-phosphorothioate RNA Antisense Oligonucleotides in the mdx Mouse Model
Auteur:
Heemskerk, Hans de Winter, Christa van Kuik, Petra Heuvelmans, Niki Sabatelli, Patrizia Rimessi, Paola Braghetta, Paola van Ommen, Gert-Jan B de Kimpe, Sjef Ferlini, Alessandra Aartsma-Rus, Annemieke van Deutekom, Judith CT