Proteasome Inhibitors Enhance Gene Delivery by AAV Virus Vectors Expressing Large Genomes in Hemophilia Mouse and Dog Models: A Strategy for Broad Clinical Application
Titel:
Proteasome Inhibitors Enhance Gene Delivery by AAV Virus Vectors Expressing Large Genomes in Hemophilia Mouse and Dog Models: A Strategy for Broad Clinical Application
Auteur:
Monahan, Paul E Lothrop, Clinton D Sun, Junjiang Hirsch, Matthew L Kafri, Tal Kantor, Boris Sarkar, Rita Tillson, D Michael Elia, Joseph R Samulski, R Jude