Biochemical, Pathological, and Skeletal Improvement of Mucopolysaccharidosis VI After Gene Transfer to Liver but Not to Muscle
Titel:
Biochemical, Pathological, and Skeletal Improvement of Mucopolysaccharidosis VI After Gene Transfer to Liver but Not to Muscle
Auteur:
Tessitore, Alessandra Faella, Armida O'Malley, Thomas Cotugno, Gabriella Doria, Monica Kunieda, Tetsuo Matarese, Giuseppe Haskins, Mark Auricchio, Alberto