Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B
Titel:
Evidence of Multiyear Factor IX Expression by AAV-Mediated Gene Transfer to Skeletal Muscle in an Individual with Severe Hemophilia B
Auteur:
Jiang, Haiyan Pierce, Glenn F. Ozelo, Margareth C. de Paula, Erich V. Vargas, Joseph A. Smith, Peter Sommer, Jürg Luk, Alvin Manno, Catherine S. High, Katherine A. Arruda, Valder R.