Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Adeno-associated Viral Vectors
Titel:
Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Adeno-associated Viral Vectors
Auteur:
Moscioni, David Morizono, Hiroki McCarter, Robert J. Stern, Adam Cabrera-Luque, Juan Hoang, Albert Sanmiguel, Julio Wu, Di Bell, Peter Gao, Guang-Ping Raper, Steven E. Wilson, James M. Batshaw, Mark L.