In Vivo Transduction by Intravenous Injection of a Lentiviral Vector Expressing Human ADA into Neonatal ADA Gene Knockout Mice: A Novel Form of Enzyme Replacement Therapy for ADA Deficiency
Titel:
In Vivo Transduction by Intravenous Injection of a Lentiviral Vector Expressing Human ADA into Neonatal ADA Gene Knockout Mice: A Novel Form of Enzyme Replacement Therapy for ADA Deficiency
Auteur:
Carbonaro, Denise A. Jin, Xiangyang Petersen, Denise Wang, Xingchao Dorey, Fred Kil, Ki Soo Aldrich, Melissa Blackburn, Michael R. Kellems, Rodney E. Kohn, Donald B.